Calcium Tolerance Genes GC-content Humoral immunity Clinical trial Immunomodulation Duchenne Impurities Immune response DMDmdx rat Immunogenicity inflammation gene therapy AAV Bioorthogonality Immunosuppression Gene transfer Intra-cerebrospinal fluid injection Inherited retinal dystrophies Manufacturing Dynamin 2 Quality control Clinical trials Insect cells Adenoassociated viral vector Gene-therapy Dose study Click chemistry Dystrophin Capsid Homologous recombination Animal model AAV Inflammation Congenital amaurosis AAV vector Capsid thermostability High-throughput sequencing Mice High-throughput technology Identity assay Assembly-activating protein DMD Discriminant analysis GRMD Childhood blindness Bioconjugates Skeletal muscle Animals AAP ABCA4 Antibody responses Ectopic expression Capsid assembly Intrathymic gene transfer CNS Gene Therapy Cerebellum AAV vectors Fluid-air exchange Homogeneity CD8 + T lymphocytes Innate immunity Beta-subunit Duchenne muscular dystrophy Cone photoreceptors CMC B-Lymphocytes/immunology/metabolism Accelerometry Crigler–Najjar Syndrome Identity Infectivity Adenoviridae/immunology Baculovirus expression vector Treg Age Cell–virus interaction Cell therapy Gene therapy In vivo Homopolymers Immune responses Antibodies/immunology/metabolism Vector Centronuclear myopathy Air tamponade Human-monocyte-derived dendritic cells Baculovirus Immunogenicity Adeno-associated virus GRMD dog Gait assessment Acute treatment Exercise Intravitreal Capsid thermal stability Analytical ultracentrifugation Engineering Gene Transfer AUC Eye surgery Exon skipping